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Sarepta Seeks Broader Approval for Gene Therapy Even After Drug Trial Fizzled
Normally when a drug fails to show a clear effect in a final-stage trial, the company developing it
2023-11-01 07:15
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Gene Therapy for Kids’ Deadly Muscle Disease Fails to Reach Trial Goal
Roche Holding AG shares dropped after a trial of its gene therapy for Duchenne muscular dystrophy did not
2023-10-31 16:57